Asian journal of pharmaceutical sciences

How lipid nanoparticles have developed to enable new kinds of gene-based medicines

Updated

Abstract

Lipid nanoparticles (LNPs) are highlighted for their superior delivery efficiency and biocompatibility in nucleic acid therapies.

  • Nucleic acid-based therapies are being explored for gene regulation and therapeutic protein production for various diseases.
  • Challenges in clinical application include high molecular weight, limited cellular uptake, and vulnerability to enzymatic degradation.
  • LNPs demonstrate significant advantages over other delivery vectors due to their customizable design and efficiency.
  • The FDA-approved siRNA drug Onpattro® serves as a key example of successful LNP application in clinical settings.
  • The review discusses recent advancements in LNP design and mechanisms, aiming to clarify their roles in overcoming delivery barriers.

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Funding

Competing interests

All authors declare they have no conflicts of interests.
PubMed

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