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Abstract
The CRISPR/Cas system may offer a new avenue for correcting genetic mutations associated with muscular dystrophies.
- Muscular dystrophies are caused by genetic mutations leading to muscle degeneration.
- The CRISPR/Cas system can edit genes, potentially allowing for permanent correction of these mutations.
- Skeletal muscle's unique structure may make it particularly responsive to CRISPR/Cas treatments.
- Challenges remain in translating CRISPR/Cas genome editing into effective therapies for muscular dystrophies.
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