International journal of nanomedicine

Safe and Effective Gene Therapy Using Non-Viral Nanoparticle Delivery

Updated

Abstract

Non-viral gene delivery systems may offer safer alternatives to viral vectors in gene therapy.

  • Non-viral platforms include lipid-based nanoparticles, polymers, dendrimers, inorganic nanocarriers, and hybrid systems.
  • These systems are associated with customizable properties and scalable manufacturing.
  • Reduced risk of adverse immune responses is a noted advantage of non-viral vectors.
  • Key parameters influencing effectiveness include cellular uptake, endosomal escape, nuclear localization, and transfection efficiency.
  • Recent preclinical and clinical studies show promising outcomes for non-viral gene delivery in various diseases, particularly cancers.

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Competing interests

0 of 7
authors report competing interests
7 report none
PubMed

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